One-off lipid-lowering gene therapy a success in world-first human trial
In a world-first trial, scientists used a one-off CRISPR gene edit to switch off a liver “fat brake” gene, slashing stubborn LDL cholesterol and triglycerides in patients whose levels refused to budge on standard treatments.
Category: Medical Innovations, Body and Mind
Tags: Heart Disease, Low-density lipoprotein (LDL) cholesterol, Cholesterol, gene therapy, clinical trials, Monash University
